Brooklyn Nets radio play-by-play voice Chris Carrino Sr. was honored by the Naismith Basketball Hall of Fame with a Curt Gowdy Media Award.

Genethon, a pioneer and leader in gene therapy for rare diseases, unveiled results at the MDA Conference in Orlando confirming the long-term efficacy of its GNT0004 gene therapy in Duchenne muscular ...

Dyne Therapeutics maintains a strong $1.1B cash position, funding operations into mid-2028 despite heavy R&D and operating ...

New analyses out to 24-months showed improvement in heart and lung function compared to expected declines in DMD natural history -- Data expand ...

FALCON is a first-in-human, open-label, multi-center Phase 1b clinical trial designed to evaluate the safety and tolerability of SGT-212 in participants aged 18-40 who have been diagnosed with FA and ...

The young girl reacts with joy and emotion as she meets Howie, her new assistance puppy, forming an instant and heartwarming bond. Annual governors' gathering with White House unraveling after Trump ...

Little Mix alum Jesy Nelson shared some personal, heartbreaking news with fans regarding her twin daughters. The 34-year-old revealed in an Instagram video posted Saturday that her 8-month-old girls, ...

The Little Mix alum welcomed daughters, Ocean Jade and Story Monroe, with her fiancé, Zion Foster, on May 15, 2025 Jesy Nelson/Instagram (2) Jesy Nelson revealed in an Instagram video that her twin ...

A genetic disorder that leads to bleeding episodes and life-threatening infections has a new FDA approved treatment, a regulatory decision that marks two notable firsts — the first gene therapy for ...

Please provide your email address to receive an email when new articles are posted on . Approximately 54% of individuals in the U.S. are affected by a neurological disorder, with headache the most ...