For columnist Alyssa Silva, advances in the development of SMA treatments have felt like glimmers of miracles.
Cure SMA is leading an advocacy campaign seeking new research funding to address unmet challenges for people with SMA.
Liver issues, including a buildup of fat in the liver, occur before the onset of neuromuscular disease, per a study in a mouse model of SMA.
Bulbar muscles, those of the face and throat, are affected in spinal muscular atrophy (SMA), and researchers in Germany found that young children with SMA cannot open their mouths as well as ...