Columnist Helen Baldwin reflects on a quarter century of changes in the SMA community and honors the memory of two ...

Spinraza treatment does not lead to significant kidney dysfunction in SMA patients with types 1 and 2, a safety and efficacy ...

For columnist Alyssa Silva, advances in the development of SMA treatments have felt like glimmers of miracles.

Cure SMA is leading an advocacy campaign seeking new research funding to address unmet challenges for people with SMA.

Liver issues, including a buildup of fat in the liver, occur before the onset of neuromuscular disease, per a study in a mouse model of SMA.

Study using a new, child-friendly scale found patients up to age 2 had smaller mouth openings than healthy peers, risking ...

Scholar Rock is asking the U.S. Food and Drug Administration to approve apitegromab for people with spinal muscular atrophy.

In surveys, parents of children with SMA and healthcare professionals in Sweden note the many ways the pandemic affected ...

Inclement weather can pose a threat to people like columnist Ari Anderson, who depend on in-home care. Such are the storms of ...