A Valentine's card exchanged reminded columnist Halsey Blocher that disabled people also deserve opportunities to serve ...
The U.S. Food and Drug Administration (FDA) has approved a new tablet formulation of Evrysdi (risdiplam), an approved oral treatment for spinal muscular atrophy (SMA).
Columnist Helen Baldwin reflects on a quarter century of changes in the SMA community and honors the memory of two ...
Spinraza treatment does not lead to significant kidney dysfunction in SMA patients with types 1 and 2, a safety and efficacy ...
Liver issues, including a buildup of fat in the liver, occur before the onset of neuromuscular disease, per a study in a mouse model of SMA.